Tag: Rare Diseases
Avance Clinical Showcases Clinical Excellence at World Orphan Drug Conference in Boston, April 23-25
North Carolina, USA & Adelaide, Australia, Apr 19, 2024 - (ACN Newswire) - Avance Clinical, the award-winning North American and Australian market-leading CRO for biotechs,...
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Scenic Biotech Announces Positive Preclinical Data for its QPCTL Inhibitor SC-2882 as Potential New Therapeutic Approach for Diffuse Large B-Cell Lymphoma
SC-2882 shows anti-lymphoma and anti-immunosuppression effect in a mouse model for diffuse large B-Cell lymphoma
Data presented today, December 9, at the 65th ASH Annual...
Adaptive optics pioneers win Rank Prize for retinal imaging breakthroughs – Physics World
Four scientists who pioneered the development of adaptive optics (AO) technologies for imaging the human retina have been awarded the 2024...
Sarepta Therapeutics Announces Third Quarter 2023 Financial Results and Recent Corporate Developments
ELEVIDYS net product revenues for the quarter totaled $69.1 million
Total revenues, which consist of net product revenues and collaboration revenues, for the third quarter...
“LEQEMBI Intravenous Infusion” (Lecanemab) Approved for the Treatment of Alzheimer’s Disease in Japan
TOKYO and CAMBRIDGE, Mass., Sept 25, 2023 - (JCN Newswire) - Eisai Co., Ltd. and Biogen Inc. announced today that humanized anti- soluble aggregated...
Pharmaceutical Temperature-Controlled Packaging Market, 2028 – Pharma TCP Market Digitization to Cut Costs and Streamline Processes – ResearchAndMarkets.com
DUBLIN–(BUSINESS WIRE)–The “Temperature-Controlled Packaging for the Pharmaceutical Market” report has been added to ResearchAndMarkets.com’s offering.
Pharmaceutical Temperature-Controlled Packaging Market is projected to reach a value...
Soligenix, Inc. CEO is Featured in an Interview with SmallCaps Daily
NEW YORK, June 29, 2023 - (ACN Newswire) - Soligenix, Inc. (NASDAQ: SNGX), a late-stage biopharmaceutical company focused on developing and commercializing products to treat rare diseases where...
The First Pangenome Map Captures the Full Scope of Human Genetic Diversity
Think of the first draft of the human genome as a book. Published just past the turn of the century, the human genome paved...
Satya Nadella wants to make Google dance in battle for AI chat-powered web search
In brief Microsoft CEO Satya Nadella has been waiting for the chance to challenge Google's dominance of internet search, and just might have finally...
AI creates high-resolution brain images from low-field strength MR scans
Portable, low-field strength MRI systems have the potential to transform neuroimaging – provided that their low spatial resolution and low signal-to-noise...
CANbridge Consolidates Gene Therapy Portfolio
Secures Exclusive Global Rights to Potentially Best-in-Class Spinal Muscular Atrophy Gene Therapy from UMass Chan Medical School
Completes Technology Transfer of Two Gene Therapies for...
Gene Therapy Is Here To Stay: Should Bigger Companies Build, Buy, Or Partner?
By Deanna Petersen, CBO of AVROBio, as part of the From the Trenches feature of LifeSciVC
Gene therapy’s tremendous potential to transform the treatment of...